Fischer M. Dominik; Simonelli Francesca; Sahni Jayashree; Holz Frank G.; Maier Rainer; Fasser Christina; Suhner Andrea; Stiehl Daniel P.; Chen Bee; Audo Isabelle; Leroy Bart P.; Khan Arif O.; Tóth-Molnár Edit; Nagy Zoltán Zsolt; Kollaborációs szervezet: PERCEIVE Study Group; et al.:
Real-World Safety and Effectiveness of Voretigene Neparvovec : Results up to 2 Years from the Prospective, Registry-Based PERCEIVE Study.
BIOMOLECULES, 14 (1).
ISSN 2218-273X
(2024)